As rare genetic disorder causes her son to regress, Carrboro mom teams up with UNC doctor studying new treatment

Hunter Syndrome is a rare genetic condition that can cause damage to the body and the brain. It often causes children to pass away in their teens, but a UNC Health ...

Ivermectin is making a post-pandemic comeback, among cancer patients

The anti-parasitic drug became a household name during the COVID-19 pandemic, and it is now being embraced as an alternative ...

SNL’s Will Forte On How Huntington’s Disease Has Become A Family Issue

Will Forte, who played MacGruber on Saturday Night Live, and his brother-in-law Doug Modling, who has Huntington's Disease, ...

Mother channels fear into advocacy after son’s rare disease diagnosis

Just days after her son was born, Julia Friar learned he had galactosemia, a rare genetic disorder that can be ...
Healio

Research advances suggest ‘bright’ treatment future for serious blood disorder

A multicenter research effort yielded findings that may allow for more effective and personalized treatment of an underrecognized but serious blood disorder.Extended follow-up of individuals with ...
News on 6

New Parkinson’s treatments may slow disease progression

About 90,000 Americans are expected to be diagnosed with Parkinson’s disease this year. Researchers say early deep brain stimulation and new therapies may help slow progression. TULSA, Okla. - About ...
Fox News

Common household plant could hold key to fighting Alzheimer's disease

A potential weapon against Alzheimer’s disease could be hidden in aloe vera, scientists recently uncovered. Aloe vera, a rubbery green plant, may be best known for its skin-soothing qualities, but a ...
Forbes

A New Treatment For Crohn’s Disease

A genetics‑guided small molecule called compound 6 gently turns down an overactive immune pathway (CARD9), offering a more precise, durable, and potentially safer treatment strategy for Crohn’s ...
Reuters

CVS Health to drop Amgen and Lilly's bone disease treatments from some drug lists

Feb 5 (Reuters) - (This Feb 5 story has been corrected to fix Prolia's 2025 sales to $4.4 billion, not $1.05 billion, in paragraph 5) Sign up here. Its pharmacy benefit management unit, Caremark, will ...
CNBC

This 11-year-old has battled a rare disease for years — a breakthrough drug helped deliver relief

To share your story, or find out how to get involved with CNBC Cures, email [email protected] Susannah Rosen was diagnosed with a KIF1A gene mutation at the age of 2½. Patients diagnosed with severe ...
Post-Bulletin

Rochester biotech firm raises $60M to fund development of liver disease treatments

ROCHESTER — Cytotheryx, a growing Rochester biotech firm working on treatments for liver disease, recently received $60 million in financing to advance its research and development. CEO Dr. John Swart ...
New Scientist

Barnacle gloop could improve inflammatory bowel disease treatments

Scientists looking to provide relief for people with inflammatory bowel disease have turned to an unusual source for inspiration: barnacles. Inflammatory bowel disease (IBD), such as Crohn’s disease ...