A new study found Spinraza treatment restores a key amino acid called taurine in SMA type 1, which may improve clinical ...
The first patient has been dosed in a Phase 1/2 study of GB221, a next-generation gene therapy for SMA type 1.
Columnist Helen Baldwin recalls the major life changes that preceded her introduction to the SMA community with the birth of ...
Medical equipment and technology are crucial for columnist Ari Anderson, who lives with SMA, so malfunctions can quickly ...
Columnist Connie Chandler enjoys volunteer work, but her physical limitations from SMA means she often needs a little help ...
In honor of Rare Disease Day, columnist Halsey Blocher shines a light on the caregivers who make life possible for those with SMA.
Blood vessel damage in the spinal cord may play a role in nerve cell loss in spinal muscular atrophy, a new study suggests.
Some results have been hidden because they may be inaccessible to you
Show inaccessible results