A new nonprofit wants to streamline gene therapy for diseases often avoided by pharmaceutical companies — making treatment ...

Autosomal dominant Alzheimer's disease (ADAD) is a genetically inherited form of Alzheimer's disease that accounts for only ...

Add Yahoo as a preferred source to see more of our stories on Google. Ancient protein networks helped scientists uncover new rare disease genes rooted in the earliest complex cells. (CREDIT: ...

Sickle cell disease causes premature aging of blood stem cells, which scientists may be able to address with a special class of drugs, according to a new study from St. Jude Children's Research ...

The origin of some neuropsychiatric diseases, such as autism, bipolar disorder, or depression, and certain neurodegenerative diseases, Alzheimer's and Parkinson's, can be found in very early stages of ...

The gene neuropilin2 encodes a receptor involved in cell-cell interactions in the brain and plays a key role in regulating the development of neural circuits. Neuropilin2 controls migration of ...

Gene therapy achieved its first major breakthroughs in the early 1990s with the treatment of a rare disease called severe combined immunodeficiency. However, the field was dealt a serious setback in ...

Initial financing led by Double Point Ventures with participation from Olive Tree Capital, Civilization Ventures and Toba Capital -- Supports ...

A new study offers insights into how the gene neuropilin2 contributes to the development of behavioral changes associated with autism spectrum disorder and epilepsy. The gene neuropilin2 encodes a ...

When a child develops kidney failure or a rare bone disorder, the cause can seem painfully immediate. It may be a single broken gene, a sudden diagnosis, or a family searching for answers. However, ...