The US Food and Drug Administration (FDA) has granted accelerated approval to Ascendis Pharma’s Yuviwel (navepegritide) for ...
Ascendis Pharma is spiraling upward by way of its TransCon platform. | Ascendis Pharma is spiraling upward by way of its TransCon platform. For the third time in six years, the Copenhagen-based ...
Yuviwel, a once-weekly injection, will now compete for market share with BioMarin’s lucrative daily shot Voxzogo.
Navepegritide is indicated for those ages 2 and older with open epiphyses ...
A Polokwane mother has launched a fund to help children with achondroplasia access a costly treatment unavailable in South Africa.
US drugmaker BioMarin Pharmaceutical today announced positive new data from studies of Voxzogo (vosoritide) in children with ...
Sanofi has halted work on a phase 2 candidate for a rare growth disorder as part of a pipeline clear-out that saw the French pharma discontinue two other rare disease assets and one of its mRNA flu ...
GLENS FALLS, N.Y. (NEWS10) – It is Physical Therapy Awareness Month and it’s also Dwarfism Awareness Month and that’s why NEWS10 was at Glens Falls Hospital’s Rehabilitation and Wellness Center.
October is a month of recognition for many in Erie and beyond. For 65,000 people in the nation born with dwarfism, the month brings awareness to their lives. Little People of America, or LPA, the ...